This information is publicly available and shared here for informational purposes only. It is not medical advice. FARA does not approve, control, or direct the research pipeline programs.

Potential treatments for FA are grouped based on mechanism of action and stage of development (in the country where the candidate is further along in its development process).

FARA helps advance treatments through funding, advocacy, patient engagement and/or collaboration. We believe that the most effective treatment is likely to be a combination of two or more treatments. To learn more about the stages of drug development, click here.

Active – programs currently under development and supported by the listed sponsor.

Inactive – programs that are no longer in development due to lack of safety or effectiveness, or where the sponsor has paused recruitment due to resource constraints and where there is no clear path forward.